Applications: Lixiprilan is the world's first approved small molecule drug that directly targets RNA, ...    More ...

Applications: Lixiprilan is the world's first approved small molecule drug that directly targets RNA, increasing the level of functional SMN protein through specific gene splicing modification. Lixiprilan can cross the blood-brain barrier and distribute in both the central and peripheral nervous systems, increasing the level of SMN protein in both areas.

7-amino-2,3-dihydro-1H-inden-4-ol;Risdiplam;RO7034067;RG7916;4H-Pyrido[1,2-a]pyrimidin-4-one,7-(4,7-diazaspiro[2.5]oct-7-yl)-2-(2,8-dimethylimidazo[1,2-b]pyridazinChemicalbook-6-yl)-;2-(2,8-dimethylimidazo[1,2-b]pyridazin-6-yl)-7-(4,7-diazaspiro[2.5]octan-7-yl)-4H-pyrido[1,2-a]pyrimidin-4-one;Risdiplam(RG-7916,RO-7034067);2H4]-Risdiplam

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